Ten-year outcome of enzyme replacement therapy with agalsidase beta in patients with Fabry disease
Crossref DOI link: https://doi.org/10.1136/jmedgenet-2014-102797
Published Online: 2015-03-20
Published Print: 2015-05
Update policy: https://doi.org/10.1136/crossmarkpolicy
Germain, Dominique P
Charrow, Joel
Desnick, Robert J
Guffon, Nathalie
Kempf, Judy
Lachmann, Robin H
Lemay, Roberta
Linthorst, Gabor E
Packman, Seymour
Scott, C Ronald
Waldek, Stephen
Warnock, David G
Weinreb, Neal J
Wilcox, William R