Ozelo, M.C.
Pasi, K.J.
Rangarajan, S.
Mitchell, N.
Lester, W.
Symington, E.
Madan, B.
Laffan, M.
Russell, C.B.
Li, M.
Kim, B.
Pierce, G.F.
Wong, W.Y.
This article is maintained by: Elsevier
Article Title: A FIRST-IN-HUMAN FOUR-YEAR FOLLOW-UP STUDY OF DURABLE THERAPEUTIC EFFICACY AND SAFETY OF AAV GENE THERAPY WITH VALOCTOCOGENE ROXAPARVOVEC FOR SEVERE HEMOPHILIA A
Journal Title: Hematology, Transfusion and Cell Therapy
CrossRef DOI link to publisher maintained version: https://doi.org/10.1016/j.htct.2020.10.099
Content Type: simple-article
Copyright: Copyright © 2020 Published by Elsevier Editora Ltda.