Kuter, D
Keel, S
Parker, C
Rees, DC
Stölzel, U
Ventura, P
Balwani, M
Gouya, L
Rhyee, S
Silver, S
This article is maintained by: Elsevier
Article Title: EIGHTEEN-MONTH INTERIM ANALYSIS OF EFFICACY AND SAFETY OF GIVOSIRAN, AN RNAI THERAPEUTIC FOR ACUTE HEPATIC PORPHYRIA, IN THE ENVISION OPEN LABEL EXTENSION
Journal Title: Hematology, Transfusion and Cell Therapy
CrossRef DOI link to publisher maintained version: https://doi.org/10.1016/j.htct.2021.10.010
Content Type: simple-article
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