One-time CRISPR Adenine Base Editing Intervention in SMA: From SMN2 Splice Correction to Motor Neuron Rescue
Crossref DOI link: https://doi.org/10.29328/journal.jgmgt.1001014
Published Online: 2026-05-27
Published Print: 2026-05-27
Update policy: https://doi.org/10.29328/crossmark-policy
Sheena P, Kochumon
Najma, Nujoom
Prem, Jagadeesan
Vinod, Scaria
DM, Vasudevan
KP, Soman
Cherupally Krishnan Krishnan, Nair
