Direct Reprogramming of Human DMD Fibroblasts into Myotubes for In Vitro Evaluation of Antisense-Mediated Exon Skipping and Exons 45–55 Skipping Accompanied by Rescue of Dystrophin Expression
Crossref DOI link: https://doi.org/10.1007/978-1-0716-4730-1_8
Published Online: 2025-07-29
Published Print: 2025
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Lee, Joshua A.
Saito, Takashi
Duddy, William
Takeda, Shin’ichi
Yokota, Toshifumi
Text and Data Mining valid from 2025-01-01
Version of Record valid from 2025-01-01
Chapter History
First Online: 29 July 2025