Antisense Oligonucleotide-Based Splice Correction of a Deep-Intronic Mutation in CHM Underlying Choroideremia
Crossref DOI link: https://doi.org/10.1007/978-3-319-75402-4_11
Published Online: 2018-05-03
Published Print: 2018
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Garanto, Alejandro
van der Velde-Visser, Saskia D.
Cremers, Frans P. M.
Collin, Rob W. J.
License valid from 2018-01-01