Is spinal muscular atrophy a disease of the motor neurons only: pathogenesis and therapeutic implications?
Crossref DOI link: https://doi.org/10.1007/s00018-015-2106-9
Published Online: 2015-12-18
Published Print: 2016-03
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Simone, Chiara
Ramirez, Agnese
Bucchia, Monica
Rinchetti, Paola
Rideout, Hardy
Papadimitriou, Dimitra
Re, Diane B.
Corti, Stefania
Funding for this research was provided by:
FP7-IRSES: “No-MND”
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