Phung, Kim
Rauch, Damian
Jackowski, Stefan
Scharke, Maya
Koujok, Khaldoun
Matzinger, Mary-Ann
Shenouda, Nazih
Jaremko, Jacob L.
Wilson, Nagwa
Jalbout, Ramy El
Santos, Rui
Khan, Nasrin
Wang, Mei
McAdam, Laura
McMillan, Hugh J.
Ma, Jinhui
Siminoski, Kerry
Ward, Leanne M. https://orcid.org/0000-0003-1557-9185
Article History
Received: 21 March 2025
Accepted: 20 August 2025
First Online: 21 October 2025
Declarations
:
: Kim Phung, Damian Rauch, Stefan Jackowski, Maya Scharke, Maya Scharke, Mary-Ann Matzinger, Nazih Shenouda, Jacob L. Jaremko, Nagwa Wilson, Ramy El Jalbout, Nasrin Khan, Mei Wang, Jinhui Ma and Kerry Siminoski have no conflicts of interest to declare.Rui Santos has been a consultant for Kyowa Kirin and QED Therapeutics Inc.Hugh J McMillan has participated in clinical trials with Roche, Italafarmaco, Dyne Therapeutics, PepGen, Regenexbio, Solid Biosciences, PTC Therapeutics, ReveraGen, Santhera, Novartis and Sarepta. He has been a consultant for Novartis Gene Therapies, Roche, Solid Biosciences, Regenexbio, and Kye Pharmaceuticals.Laura McAdam has participated in clinical trials with Italafarmaco and been a consultant to Kye Pharmaceuticals and Acadia Pharmaceuticals.Leanne M. Ward has participated in clinical trials with Edgewise Therapeutics, Catalyst, ReveraGen and Roche (with funds to Dr. Ward’s institution), and been a consultant to Edgewise Therapeutics, Santhera, Kye Pharmaceuticals, and Roche (with funds to Dr. Ward’s institution).