Nasomyont, Nat https://orcid.org/0000-0001-8996-8760
Tian, Cuixia
Hornung, Lindsey
Khoury, Jane
Wong, Brenda L.
Rutter, Meilan M.
Article History
Received: 24 October 2025
Accepted: 15 March 2026
First Online: 30 March 2026
Declarations
:
: N.N., L.H., J.K., and B.W. have no conflicts of interest to declare. C.T. has been a site PI for clinical trials and studies sponsored by Avexis, BioHaven, Bristol Myers Squibb, Capricor, Catabasis, FibroGen, Pfizer, PTC Therapeutics, Roche, Santhera, and Sarepta and has been a consultant for Biogen, Catalyst, Entrada, Regenxbio, Sarepta, and Solid Bioscience. M.R. has served as a consultant for Catalyst Pharmaceuticals, Inc.