Capasso, Anna
Arpaia, Chiara
Panicucci, Chiara
Gulli, Consolato
Villa, Marianna
Repetto, Agnese
Coratti, Giorgia
Morando, Simone
Cicala, Gianpaolo
Oliva, Alessandro
Milardi, Domenico
Cipolla, Clelia
Catapano, Gennaro
Marzoli, Anna
Damasio, Maria Beatrice
Brogna, Claudia
Palermo, Concetta
Di Iorgi, Natascia
Bruno, Claudio
Ficociello, Luana
Gaudino, Simona
Pane, Marika
Ward, Leanne M.
Mercuri, Eugenio https://orcid.org/0000-0002-9851-5365
Funding for this research was provided by:
Fondazione Telethon (GUP23005)
Tier 1 Wall Street
Università Cattolica del Sacro Cuore
Article History
Received: 5 January 2026
Accepted: 26 March 2026
First Online: 17 April 2026
Declarations
:
: The study was approved by the Ethics committee (Protocol 600014186/17).
: Written informed consent was obtained in all cases.
: GC participated to Advisory Board for Italfarmaco, ROCHE and Sarepta; CB, participated to Advisory Board for ROCHE; EM participated to Advisory Board for ROCHE, Sarepta, PTC, Italfarmaco, Pfizer, Dyne, NS Pharma, Santhera, Avidity, Entrada, Edgewise and Solid. MP participated to Advisory Board for ROCHE, Sarepta, PTC, Italfarmaco, Pfizer and Dyne; The remaining authors have nothing to disclose.