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Authors
Windels, Oskar https://orcid.org/0009-0006-7522-4887
Simon, Alexander https://orcid.org/0000-0003-3325-8983
Muschol, Nicole https://orcid.org/0000-0003-4213-7294
Yorgan, Timur https://orcid.org/0000-0002-0712-0983
Barvencik, Florian https://orcid.org/0000-0002-0200-8431
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Funding
Funding for this research was provided by:
Deutsche Forschungsgemeinschaft (517063424)
Universitätsklinikum Hamburg-Eppendorf (UKE)
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Article History
Received: 26 November 2025
Accepted: 14 April 2026
First Online: 25 April 2026
Declarations
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: This study has been performed in accordance with the 1964 Declaration of Helsinki and its later amendments, and approval for this project was obtained from the local ethics committee (Ethikkomission der Ärztekammer Hamburg, PV5364).
: Written informed consent was obtained from the patient.
: AS and TY state that they have no conflict of interest. NM has received travel support, consulting fees and/or honoraria from Amicus, BioMarin Pharmaceutical, Chiesi, GC Biopharma, JCR Pharmaceuticals, Sanofi Genzyme, Takeda, Ultragenyx, and Regenxbio. OW has received a travel grant from Inozyme, FB has received honoraria, served as a speaker, and acted as a consultant for Alexion, Diasorin, Blueprint Medicines (Germany) GmbH, UCB, and FOMF GmbH Forum für medizinische Fortbildung, and has received institutional research grants from Alexion and UCB.
