Wordsworth, Paul http://orcid.org/0000-0001-7512-3468
Chan, Marian
Article History
Received: 29 January 2019
Accepted: 16 March 2019
First Online: 15 April 2019
Compliance with Ethical Standards
:
: Paul Wordsworth and Marian Chan declare that they have no conflict of interest.
: Patients were recruited following informed consent to the Rare UK Disease Study (RUDY - ratified by South Central Research Ethics Committee, LREC14/SC/0126).