Morton, Terri L. http://orcid.org/0000-0002-5004-8761
Laskin, Oscar L.
Kaushik, Diksha
Lee, Lucy
Ma, Jiyuan
Bar, Cristian M.
Kristensen, Allan
O’Keefe, Kylie
Golden, Lee
Klein, Matthew
Kong, Ronald http://orcid.org/0000-0002-4692-7499
Funding for this research was provided by:
PTC Therapeutics
Article History
Received: 13 December 2022
Accepted: 22 May 2023
First Online: 6 June 2023
Declarations
:
: The study was conducted in accordance with the principles outlined in the 1964 Declaration of Helsinki and its later amendments and the International Conference on Harmonisation Good Clinical Practice. The Independent Ethics Committee of the Foundation for Evaluation of Ethics in Biomedical Research (The Netherlands) reviewed and approved the clinical study protocol, any clinical study protocol amendments, subject information sheets, written informed consent forms, and other relevant documentation.
: Before participating in the study, each subject was apprised of the nature and purpose of the study, and written informed consent was obtained.
: All authors have reviewed and approved of publishing this manuscript.
: All authors are employees of PTC and all hold stock in the company, with the exception of Oscar Laskin who is a consultant to PTC and Cristian Bar who is employed by Syneos Health.