Neal, Ashley E. https://orcid.org/0000-0002-6922-5414
Barker, Piers C. A.
Dunbar, Colin II
Goot, Benjamin
Ralston, Tracy
Richards, Bernadette
Sarkar, Indrani
Shreve, Sara
Tseng, Stephanie Y.
Hill, Garick D.
Article History
Received: 7 August 2025
Accepted: 1 October 2025
First Online: 17 October 2025
Declarations
:
: Garick Hill – consultant for Ultragenyx.