Averill, Lauren W. https://orcid.org/0000-0003-0734-9611
Kecskemethy, Heidi H.
Theroux, Mary C.
Mackenzie, William G.
Pizarro, Christian
Bober, Michael B.
Ditro, Colleen P.
Tomatsu, Shunji
Article History
Received: 23 June 2020
Revised: 21 September 2020
Accepted: 16 December 2020
First Online: 20 February 2021
Compliance with ethical standards
:
: Dr. Mackenzie has received a grant from Biomarin and is on the Little People of America Medical Advisory Board. Dr. Bober is a consultant and site primary investigator for Biomarin.