Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat
Crossref DOI link: https://doi.org/10.1007/s00256-014-1891-9
Published Online: 2014-05-10
Published Print: 2014-10
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Kamath, Ravi S.
Lukina, Elena
Watman, Nora
Dragosky, Marta
Pastores, Gregory M.
Arreguin, Elsa Avila
Rosenbaum, Hanna
Zimran, Ari
Aguzzi, Rasha
Puga, Ana Cristina
Norfleet, Andrea M.
Peterschmitt, M. Judith
Rosenthal, Daniel I.
License valid from 2014-05-10