Kim, Aimee G.
Upah, Sydney A.
Brandsema, John F.
Yum, Sabrina W.
Blinman, Thane A. http://orcid.org/0000-0001-9351-3187
Article History
Accepted: 10 January 2019
First Online: 7 February 2019
Compliance with ethical standards
:
: JFB is a consultant for Biogen, Avexis, PTC Therapeutics, Sarepta, Alexion, Cytokinetics, and Marathon, and is a speaker for Biogen. SWY is a member of the advisory board for PTC Therapeutics. The remaining authors declare that they have no conflicts of interest.
: All procedures performed in studies involving human participants were in accordance with the ethical standards of the institutional and/or national research committee and with the 1964 Helsinki declaration and its later amendments or comparable ethical standards.
: The study was conducted under a waiver of consent (parental permission) per 45 CFR 46.116(d), a waiver of assent per 45 CFR 46.408(a), and a waiver of HIPAA authorization per 45 CFR 164.512(i)(2)(ii).