Marques, Christine
Held, Aaron
Dorfman, Katherine
Sung, Joon
Song, Catherine
Kavuturu, Amey S.
Aguilar, Corey
Russo, Tommaso
Oakley, Derek H.
Albers, Mark W.
Hyman, Bradley T.
Petrucelli, Leonard
Lagier-Tourenne, Clotilde
Wainger, Brian J. http://orcid.org/0000-0002-3664-7231
Funding for this research was provided by:
The ALS Association (21-PDF-564)
National Institutes of Health (F32NS114319, DP2-NS106664, RF1NS127407)
New York Stem Cell Foundation (NYSCF-I-R44)
Article History
Received: 9 August 2023
Revised: 15 December 2023
Accepted: 9 January 2024
First Online: 13 March 2024
Declarations
:
: The authors declare the following competing interests. B.T.H. has a family member who works at Novartis and owns stock in Novartis; he serves on the SAB of Dewpoint and owns stock. He serves on a scientific advisory board or is a consultant for AbbVie, Aprinoia Therapeutics, Arvinas, Avrobio, Axial, Biogen, BMS, Cure Alz Fund, Cell Signaling, Eisai, Genentech, Ionis, Latus, Novartis, Sangamo, Sanofi, Seer, Takeda, the US Dept. of Justice, Vigil, and Voyager. His laboratory is supported by research grants from the National Institutes of Health, Cure Alzheimer’s Fund, Tau Consortium, and the JPB Foundation and sponsored research agreements from Abbvie, BMS, and Biogen. L.P. and Mayo Clinic have licensed technology involving <i>C9orf72</i> repeat expansion constructs and a virus and AAV-C9orf72-149 repeat expansion mouse model. L.P. is a consultant for Expansion Therapeutics. M.W.A. owns shares and is on the scientific advisory board of Aromha, Inc. He serves on the scientific advisory board of Sudo Therapeutics and is a consultant for BMS and Transposon. C.L.T. serves as a scientific advisory board member or is a consultant for Arbor Biotechnology, Dewpoint Therapeutics, Libra Therapeutics, Mitsubishi Tanabe Pharma Corporation, Sanofi, and SOLA Biosciences. B.J.W. serves as a scientific advisory board member and a consultant for Quralis and is a consultant for Apic Bio, Q-State Biosciences, Takeda, and Sanofi. The remaining authors declare no competing interests.