Clay, Alexandra
Obrochta, Kristin M. https://orcid.org/0000-0002-6090-7013
Soon, Russell K. Jr
Russell, Christopher B. https://orcid.org/0000-0002-0240-1815
Lynch, David R. https://orcid.org/0000-0001-7168-214X
Funding for this research was provided by:
Friedreich's Ataxia Research Alliance (0001)
Article History
Received: 24 February 2020
Revised: 26 April 2020
Accepted: 28 April 2020
First Online: 8 May 2020
Compliance with ethical standards
:
: Dr Lynch and Ms Clay report no conflicts. KMO, CBR, and RKS are employees and shareholders in BioMarin Pharmaceutical Inc., CBR is a former employee and shareholder of Amgen.
: This works was approved by the Children’s Hospital of Philadelphia and Sanguine Biosciences Inc. IRBs.
: All subjects signed written informed consent.
: All authors have reviewed the final work.
: Results will be deposited in the Critical Path Institute on completion and publication.<b>Code availability</b> (N/A).