Scaravilli, Alessandra
Gabusi, Ilaria
Mari, Gaia
Battocchio, Matteo
Bosticardo, Sara
Schiavi, Simona
Bender, Benjamin
Kessler, Christoph
Brais, Bernard
La Piana, Roberta
van de Warrenburg, Bart P.
Cosottini, Mirco
Timmann, Dagmar
,
Daducci, Alessandro
Schüle, Rebecca
Synofzik, Matthis
Santorelli, Filippo Maria
Cocozza, Sirio http://orcid.org/0000-0002-0300-5160
Funding for this research was provided by:
Deutsche Forschungsgemeinschaft (441409627)
European Joint Programme on Rare Diseases (825575)
Università degli Studi di Napoli Federico II
Article History
Received: 3 May 2024
Revised: 4 June 2024
Accepted: 7 June 2024
First Online: 16 June 2024
Declarations
:
: SC have received fees for Advisory Board by Amicus. All other co-authors have no possible financial conflict of interest to declare.
: The study was approved by local Ethics Committee of each center and written informed consent was obtained from each participant.