van der Zwaan, K. F. https://orcid.org/0000-0002-5532-5553
Feleus, S. https://orcid.org/0000-0002-1160-0920
Dekkers, O. M. https://orcid.org/0000-0002-1333-7580
Roos, R. A. C. https://orcid.org/0000-0001-5591-1133
de Bot, S. T. https://orcid.org/0000-0002-3512-2468
Article History
Received: 25 July 2024
Revised: 17 October 2024
Accepted: 22 October 2024
First Online: 15 January 2025
Declarations
:
: O.M. Dekker is Deputy Editor European Journal of Endocrinology. R.A.C. Roos is member of the DSMB uniQure CT-AMT 130, DSMB Enroll-HD. Susanne T. de Bot is a member of the HD Expert Advisory Panel for the PTC518 phase 3 program (PTC Therapeutics).
: This study was conducted in compliance with the ethical standards outlined in the Declaration of Helsinki. All sites obtained and maintained local ethical approval. All participants provided informed consent prior to participation in the study, and their confidentiality and privacy were maintained throughout.