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Authors
Wenninger, Stephan https://orcid.org/0000-0001-8407-3642
Heidsieck, Eva
Wirner-Piotrowski, Corinna
Mijic, Marko
Garcia-Angarita, Natalia
Gutschmidt, Kristina
Mendelshohn, Daniel H.
Schoser, Benedikt
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Funding
Funding for this research was provided by:
Deutsche Gesellschaft für Muskelkranke e.V.
Klinikum der Universität München
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Article History
Received: 6 June 2025
Revised: 22 August 2025
Accepted: 25 August 2025
First Online: 11 September 2025
Declarations
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: All authors report no disclosures regarding this study. Outside of this context, SW has received research grant from the DGM – Deutsche Gesellschaft für Muskelkranke e.V. He has served on advisory boards for Alexion Pharma, CSL Behring, and Sanofi Genzyme GmbH. He received funding for travel or speaker honoraria from Sanofi-Aventis Germany GmbH; SH Glykogenose Gesellschaft; AbbVie Germany GmbH; Recordati Pharma GmbH; CSL Behring GmbH; Alexion Pharma GmbH; Desitin Germany; Akcea GmbH. Outside of this context, BS has served on advisory boards for Alexion, Argenex, Amicus, Astellas, Spark, and Sanofi; he has undertaken contracted unrestricted research for Sanofi and Amicus; and has received honoraria from Kedrion. The other authors have no conflicts of interest to declare.
: The study was approved by the ethics committee of the LMU Klinikum, Project No. 19-330, and the protocol was registered on a public clinical trials registry (ClinicalTrials.gov Identifier NCT04052958).
