Funding for this research was provided by:
Ministero dell’Istruzione, dell’Università e della Ricerca (20122EK9SZ)
Text and Data Mining valid from 2019-02-26
Received: 18 October 2018
Revised: 5 February 2019
Accepted: 6 February 2019
First Online: 26 February 2019
Compliance with ethical statements
: MS received educational grants and travel grants from BioMarin, Chiesi, Genzyme, and Shire. DC received travel grants from BioMarin, Genzyme, and Shire. AZ, FD, LR, AR, RB, NV, LS, SL, FB, and RT declare no conflicts of interest.
: All procedures involving humans performed in the study were in accordance with the ethical standards of the institutional research committee and with the 1964 Helsinki declaration and its later amendments.
: Informed consent was obtained from all individual participants included in the study.