el Manouni el Hassani, Sofia http://orcid.org/0000-0002-2806-444X
Niemarkt, Hendrik J.
Derikx, Joep P. M.
Berkhout, Daniel J. C.
Ballón, Andrea E.
de Graaf, Margot
de Boode, Willem P.
Cossey, Veerle
Hulzebos, Christian V.
van Kaam, Anton H.
Kramer, Boris W.
van Lingen, Richard A.
Vijlbrief, Daniel C.
van Weissenbruch, Mirjam M.
Benninga, Marc A.
de Boer, Nanne K. H.
de Meij, Tim G. J.
Funding for this research was provided by:
Stichting Zeldzame Ziekten Fonds
Article History
Received: 7 April 2020
Revised: 17 November 2020
Accepted: 23 November 2020
First Online: 2 December 2020
Compliance with ethical standards
:
: The authors declare that they have no conflict of interest
: The local institutional review boards of all nine participating centers granted approval (2014.386 amendment A2016.363).
: Informed consent was obtained from all individual participants included in the study.
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