Bierlaagh, Marlou C.
Muilwijk, Danya
Beekman, Jeffrey M.
van der Ent, Cornelis K.
Article History
Received: 21 April 2021
Revised: 13 June 2021
Accepted: 15 June 2021
First Online: 2 July 2021
Declarations
:
: CKvdE and JMB report grants from Eloxx, Galapagos NV, Gilead, GSK, Nutricia, ProQR, Proteostasis, Teva, and Vertex Pharmaceuticals Incorporated, and a patent (10006904) with royalties paid.