Weitz, Marcus
Laube, Guido F.
Schmidt, Maria
Krupka, Kai
Murer, Luisa
Müller, Dominik
Hoppe, Bernd
Büscher, Anja
König, Jens
Pohl, Martin
Jungraithmayr, Therese
Thiel, Florian
Billing, Heiko
Grenda, Ryszard
Rubik, Jacek
Kaabak, Michael M.
Yalcinkaya, Fatos
Topaloglu, Rezan
Webb, Nicholas
Dello Strologo, Luca
Pape, Lars
Nadalin, Silvio
Tönshoff, Burkhard
Article History
Received: 10 October 2017
Revised: 3 January 2018
Accepted: 4 January 2018
First Online: 13 March 2018
Compliance with ethical standards
:
: Marcus Weitz has participated on an Advisory Board for Astellas and has received lecture fees from Alexion. Burkhard Tönshoff has received research grants, travel grants and lecture fees and participated in advisory boards of Astellas, Bristol-Myers Squibb, Novartis and Roche. Heiko Billing has received travel grants by Astellas. Lars Pape has received research grants, travel grants and lecture fees, participated in advisory boards of Astellas and Novartis and has received research grants and travel grants from Sanofi. Michael Kabaak received research grants and lecture fees and participated in the advisory board of Astellas and Alexion. Luca DelloStrologo has received lecture fees from Novartis. Nicholas Webb participated on Advisory Boards for Abbvie, Astellas, Alexion and Raptor. The other contributing authors declare that they have no conflict of interest.
: All procedures performed in studies involving human participants were in accordance with the ethical standards of the institutional and/or national research committee and with the 1964 Helsinki declaration and its later amendments or comparable ethical standards. Written informed consent to participate in the registry was obtained by all parents or guardians and patients when appropriate for their age.