Brown, Denver D. https://orcid.org/0000-0003-3381-0336
Roem, Jennifer
Ng, Derek K.
Coghlan, Ryan F.
Johnstone, Brian
Horton, William
Furth, Susan L.
Warady, Bradley A.
Melamed, Michal L.
Dauber, Andrew
,
Warady, Bradley
Furth, Susan
Schwartz, George
Muñoz, Alvaro
Ng, Derek
Funding for this research was provided by:
Eunice Kennedy Shriver National Institute of Child Health and Human Development (K12HD00139)
Article History
Received: 2 February 2023
Revised: 16 May 2023
Accepted: 7 June 2023
First Online: 19 July 2023
Declarations
:
: A.D consults for Ascendis, Novo Nordisk, BridgeBio, and Biomarin. The remaining authors have no relevant disclosures.