Müller, Sophia
Kluck, Rika
Jagodzinski, Celina
Brügelmann, Malina
Hohenfellner, Katharina
Büscher, Anja
Kemper, Markus J.
Fröde, Kerstin
Oh, Jun
Billing, Heiko
Thumfart, Julia
Weber, Lutz T.
Acham-Roschitz, Birgit
Arbeiter, Klaus
Tönshoff, Burkhard
Hagenberg, Martina
Pavičić, Leo
Haffner, Dieter
Zivicnjak, Miroslav http://orcid.org/0000-0001-9302-712X
Funding for this research was provided by:
Horizon Pharmaceuticals
Medizinische Hochschule Hannover (MHH)
Article History
Received: 13 March 2023
Revised: 9 June 2023
Accepted: 13 June 2023
First Online: 7 July 2023
Declarations
:
: The study received appropriate Ethics Committee approval from the Institutional Review Board at each site and was performed in accordance with the Declaration of Helsinki.
: Written informed consent was obtained from all parents/guardians, with consent or assent from patients when appropriate for their age.
: Dieter Haffner received speaker fees and research grants from Horizon and Chiesi. Jun Oh received speaker fees from Horizon and Chiesi. Burkhard Tönshoff participated in advisory boards for Chiesi. Julia Thumfart received speaker fees from Horizon. Lutz T. Weber received speaker fees from Chiesi. KH was supported by the Cystinosis Foundation Germany.All other authors declare that they have no conflict of interest.