Amoroso, Loredana https://orcid.org/0000-0003-1950-4754
Fagioli, Franca https://orcid.org/0000-0002-9257-900X
Tondo, Annalisa https://orcid.org/0000-0003-2784-5487
Conte, Massimo https://orcid.org/0000-0001-9405-7339
Badino, Clara https://orcid.org/0000-0002-2714-6494
Di Cataldo, Andrea https://orcid.org/0000-0002-4509-3066
Viscardi, Elisabetta https://orcid.org/0000-0002-6128-4655
De Leonardis, Francesco https://orcid.org/0000-0001-5801-7225
De Ioris, Maria Antonietta https://orcid.org/0000-0002-2113-4505
Luksch, Roberto https://orcid.org/0000-0002-7203-4176
Funding for this research was provided by:
EUSA Pharma
Recordati Rare Diseases
Article History
Received: 19 March 2024
Accepted: 30 December 2024
First Online: 5 February 2025
Declarations
:
: N/A.
: N/A.
: The authors were consultants on a board for EUSA Pharma/Recordati Rare Diseases.