Early experience with compassionate use of 2 hydroxypropyl-beta-cyclodextrin for Niemann–Pick type C disease: review of initial published cases
Crossref DOI link: https://doi.org/10.1007/s10072-017-2833-9
Published Online: 2017-02-02
Published Print: 2017-05
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Megías-Vericat, Juan Eduardo
García-Robles, Ana
Company-Albir, María José
Fernández-Megía, María José
Pérez-Miralles, Francisco Carlos
López-Briz, Eduardo
Casanova, Bonaventura
Poveda, José Luis
License valid from 2017-02-02