Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo‐controlled study
Crossref DOI link: https://doi.org/10.1007/s10545-014-9715-6
Published Online: 2014-05-09
Published Print: 2014-11
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Hendriksz, Christian J.
Burton, Barbara
Fleming, Thomas R.
Harmatz, Paul
Hughes, Derralynn
Jones, Simon A.
Lin, Shuan‐Pei
Mengel, Eugen
Scarpa, Maurizio
Valayannopoulos, Vassili
Giugliani, Roberto
,
Slasor, Peter
Lounsbury, Debra
Dummer, Wolfgang
Version of Record valid from 2014-05-09