Vockley, Jerry
Burton, Barbara
Berry, Gerard T.
Longo, Nicola
Phillips, John
Sanchez‐Valle, Amarilis
Tanpaiboon, Pranoot
Grunewald, Stephanie
Murphy, Elaine
Bowden, Alexandra
Chen, Wencong
Chen, Chao‐Yin
Cataldo, Jason
Marsden, Deborah
Kakkis, Emil
Funding for this research was provided by:
Ultragenyx Pharmaceutical
National Medical Center
University of South Florida
Vanderbilt University Medical Center
University of Utah
Ultragenyx Pharmaceutical
Ultragenyx Pharmaceutical (UX007‐CL201)
Publication History
Published: 2019-02-11