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Authors
Topal, Joseph
Panchal, Neelam
Barroeta, Amairelys
Roppelt, Anna
Mudde, Annelotte
Gaspar, H. Bobby
Thrasher, Adrian J.
Houghton, Benjamin C.
Booth, Claire https://orcid.org/0000-0002-2626-5037
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Funding
Funding for this research was provided by:
Action Medical Research (GN2761)
Medical Research Council
Great Ormond Street Hospital Charity
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Article History
Received: 22 August 2022
Accepted: 19 October 2022
First Online: 3 November 2022
Change Date: 1 October 2025
Change Type: Update
Change Details: In this article, the Funder ID was incorrectly listed as 'Medical Research Foundation: 10.13039/501100009187.' It should be 'Medical Research Council: 10.13039/501100000265.'
Declarations
:
: Ethical approval in place.
: Informed consent was obtained from the patient and/or parents of each patient for research samples, and patients were treated in accordance with the Declaration of Helsinki.
: HBG is an employee of Orchard Therapeutics and holds equity in the company.
