Hoffmann, Marie-Christin
Cavalli, Giulio
Fadle, Natalie
Cantoni, Eleonora
Regitz, Evi
Fleser, Octavian
Klemm, Philipp
Zaks, Marina
Stöger, Elisabeth
Campochiaro, Corrado
Tomelleri, Alessandro
Baldissera, Elena
Bittenbring, Jörg Thomas
Zimmer, Vincent
Pfeifer, Jochen
Fischer, Yvan
Preuss, Klaus-Dieter
Bewarder, Moritz
Thurner, Bernhard
Fuehner, Sabrina
Foell, Dirk
Dagna, Lorenzo
Kessel, Christoph
Thurner, Lorenz http://orcid.org/0000-0002-8167-2989
Funding for this research was provided by:
Universität des Saarlandes (BioNanoMed)
Universitätsklinikum des Saarlandes und Medizinische Fakultät der Universität des Saarlandes
Article History
Received: 17 August 2023
Accepted: 17 December 2023
First Online: 17 January 2024
Declarations
:
: This study was approved by the local Ethical Review Boards (Ärztekammer des Saarlandes: 41/21) (Münster 2015–670-fS) (Milano STS-CE 065/8) and conducted according to the Declaration of Helsinki. All parents and patients provided written informed consent.
: GC was recruited by Novartis after executing the study and writing the first draft and is presently an associate of Novartis. DF received speaker fees/honoraria from Chugai-Roche, Novartis, and SOBI, as well as research support from Novartis, Pfizer, and SOBI. CK has received consulting fees from Novartis and Swedish Orphan Biovitrum (SOBI) (< US$10,000 each) and receives research support from Novartis (> US$10,000). LTh received travel grants from Abbvie and consultancy Astra-Zeneca and Incyte (less than US$10,000 each). The other authors declare that they have no competing interests.