Conrado, Daniela J.
,
Larkindale, Jane
Berg, Alexander
Hill, Micki
Burton, Jackson
Abrams, Keith R.
Abresch, Richard T.
Bronson, Abby
Chapman, Douglass
Crowther, Michael
Duong, Tina
Gordish-Dressman, Heather
Harnisch, Lutz
Henricson, Erik
Kim, Sarah
McDonald, Craig M.
Schmidt, Stephan
Vong, Camille
Wang, Xiaoxing
Wong, Brenda L.
Yong, Florence
Romero, Klaus
Article History
Received: 21 January 2019
Accepted: 15 May 2019
First Online: 24 May 2019
Compliance with ethical standards
:
: The D-RSC Consortium includes Biophytis, Catabasis Pharmaceuticals, Mallinckrodt, Pfizer, Santhera Pharmaceuticals, Sarepta Therapeutics and Wave Life Sciences. The ImagingDMD Network is funded through NIH Grant RO1AR056973. KRA has served as a paid consultant, providing methodological advice, to; Abbvie, Amaris, Allergan, Astellas, AstraZeneca, Boehringer Ingelheim, Bristol-Meyers Squibb, Creativ-Ceutical, GSK, ICON/Oxford Outcomes, Ipsen, Janssen, Eli Lilly, Merck, NICE, Novartis, NovoNordisk, Pfizer, PRMA, Roche and Takeda, and has received research funding from Association of the British Pharmaceutical Industry (ABPI), European Federation of Pharmaceutical Industries & Associations (EFPIA), Pfizer and Sanofi. He is a Partner and Director of Visible Analytics Limited, a healthcare consultancy company. CMM has served as a consultant for clinical trials for PTC Therapeutics, and outside the submitted work as a consultant for Biomarin, Sarepta, Eli Lilly, Pfizer, Santhera Pharmaceuticals, Cardero Therapeutics, Inc., Catabasis, Capricor Therapeutics, Astellas and FibroGen; serves on external advisory boards related to Duchenne muscular dystrophy for PTC Therapeutics, Eli Lilly, Sarepta Therapeutics, Santhera Pharmaceuticals, and Capricor; and reports grants from US Dept. of Education/NIDRR, NIDILRR, US NIH/NIAMS, US Dept. of Defense, and Parent Project Muscular Dystrophy US, during the conduct of the study. Project HERCULES, which supported MH, KRA and MC, is funded by Duchenne UK, Pfizer, PTC Therapeutics, Roche, Summit Therapeutics PLC, Sarepta Therapeutics Inc, Wave Life Sciences USA Inc, Solid Biosciences, Santhera Pharmaceuticals and Catabasis Pharmaceuticals.” MC has served as a paid consultant, providing methodological advice, to ICON/Oxford Outcomes and Roche. DChapman, LH and CV are employees and shareholders of Pfizer.