How close are we to therapies for Sanfilippo disease?
Crossref DOI link: https://doi.org/10.1007/s11011-017-0111-4
Published Online: 2017-09-18
Published Print: 2018-02
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Gaffke, Lidia
Pierzynowska, Karolina
Piotrowska, Ewa
Węgrzyn, Grzegorz http://orcid.org/0000-0003-4042-7466
Funding for this research was provided by:
Fundacja Sanfilippo (1/2017)
License valid from 2017-09-18