Gadelha, Mônica R.
Wildemberg, Luiz Eduardo
Shimon, Ilan
Article History
Accepted: 21 May 2022
First Online: 7 June 2022
Competing interests
: MRG has received speaker fees from Recordati Rare Diseases, attended Recordati Rare Diseases advisory boards, and is principal investigator in clinical trials from Recordati Rare Diseases and Novartis. LEW has received speaker fees from Novartis and participates as a sub-investigator in Recordati Rare Diseases and Novartis clinical trials. IS has received speaker fees from Novartis and Medison, attended Novartis advisory board, and participated as an investigator in Novartis and Strongbridge Pharma clinical trials.