Revenfeld, Anne Louise S.
Møller, Anaïs M. J.
Tylvad, Mette
Bill, Marie
Rosenberg, Carina A.
Møller, Bjarne K.
Funding for this research was provided by:
Bloddonorerne i Danmark (FF 2022/02)
Innovationsfonden (8056-00010A)
Article History
Received: 23 September 2025
Accepted: 16 December 2025
First Online: 26 December 2025
Declarations
:
: All study participants provided consent for publication through signed consent form, prior to study inclusion.
: The study was carried out based on an approved protocol entitled “Korrektion af den genetiske baggrund for livstruende immundefekt ved gen-editering og ekspansion af bloddannende stamceller”. The approval was granted by The Central Denmark Region Committees on Health Research Ethics with approval number 1-10-72-144-19, approval date Dec 7th 2022.
: The authors declare no competing interests.
: Not applicable.