The Case for the Use of Patient and Caregiver Perception of Change Assessments in Rare Disease Clinical Trials: A Methodologic Overview
Crossref DOI link: https://doi.org/10.1007/s12325-019-00920-x
Published Online: 2019-03-16
Published Print: 2019-05
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Contesse, Marielle G.
Valentine, James E.
Wall, Tracy E.
Leffler, Mindy G.
Funding for this research was provided by:
Stealth BioTherapeutics
Article History
Received: 22 January 2019
First Online: 16 March 2019