NiMhurchadha, Sinead https://orcid.org/0000-0001-9441-6899
Butler, Karen https://orcid.org/0000-0002-2335-6064
Argent, Rob https://orcid.org/0000-0002-3522-9409
Palm, Katja https://orcid.org/0000-0003-4383-266X
Baujat, Genevieve https://orcid.org/0000-0001-7435-0298
Cormier-Daire, Valerie https://orcid.org/0000-0002-2839-9856
Mohnike, Klaus https://orcid.org/0000-0001-5113-8657
Funding for this research was provided by:
BioMarin Pharmaceutical
Article History
Received: 21 February 2023
Accepted: 14 March 2023
First Online: 5 April 2023