Document is current

Article History

Received: 4 April 2025

Accepted: 3 July 2025

First Online: 25 July 2025

Declarations

:

: Aliya A. Khan has received honoraria from Amgen and Alexion and support from Ascendis, Calcilytix, Amolyt, and Alexion, AstraZeneca Rare Disease. Eric T. Rush has received consulting fees, support for attending meetings, and honoraria from Alexion, AstraZeneca Rare Disease. He is also on the Alexion advisory board and his institution has received grants from Alexion, AstraZeneca Rare Disease. Craig Wakeford and Daniel Staub are employees of and may own stock/options in Alexion, AstraZeneca Rare Disease. Maria Luisa Brandi has received consulting fees, support for attending meetings, and honoraria from Alexion, AstraZeneca Rare Disease. She is also on the Alexion advisory board and her institution has received grants from Alexion, AstraZeneca Rare Disease.

: This review article did not require institutional review board or institutional animal care and use committee approval, as it is based on previously conducted studies and does not contain any new studies with human participants or animals performed by any of the authors.