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Expression of a Secretable, Cell-Penetrating CDKL5 Protein Enhances the Efficacy of Gene Therapy for CDKL5 Deficiency Disorder

Crossref DOI link: https://doi.org/10.1007/s13311-022-01295-8

Published Print: 2022-10

Update policy: https://doi.org/10.1016/elsevier_cm_policy

Authors

Medici, Giorgio

Tassinari, Marianna

Galvani, Giuseppe

Bastianini, Stefano

Gennaccaro, Laura

Loi, Manuela

Mottolese, Nicola

Alvente, Sara

Berteotti, Chiara

Sagona, Giulia

Lupori, Leonardo

Candini, Giulia

Baggett, Helen Rappe

Zoccoli, Giovanna

Giustetto, Maurizio

Muotri, Alysson

Pizzorusso, Tommaso

Nakai, Hiroyuki

Trazzi, Stefania

Ciani, Elisabetta https://orcid.org/0000-0003-3130-5168
Funding

Funding for this research was provided by:

Fondazione Telethon (GGP19045)

Fondation Jérôme Lejeune

Orphan Disease Center, Perelman School of Medicine, University of Pennsylvania

Alma Mater Studiorum - Università di Bologna
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Text and Data Mining valid from 2022-10-01

Version of Record valid from 2022-09-15
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This article is maintained by: Elsevier

Article Title: Expression of a Secretable, Cell-Penetrating CDKL5 Protein Enhances the Efficacy of Gene Therapy for CDKL5 Deficiency Disorder

Journal Title: Neurotherapeutics

CrossRef DOI link to publisher maintained version: https://doi.org/10.1007/s13311-022-01295-8

Content Type: article

Copyright: Copyright © 2022 The Author(s). Published by Elsevier B.V. All rights reserved.