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Article History

Accepted: 18 December 2023

First Online: 23 January 2024

Declarations

:

: This study was funded by Sarepta Therapeutics Inc.

: IA and KG are employees of Sarepta Therapeutics Inc (no grant number). KMJ, JD, and SMS are employees of Broadstreet HEOR, which received funds from Sarepta to conduct this study. DF, PN, and DCM received consulting fees related to this work. DF has a proprietary interest in Health Utilities Incorporated, Dundas, Ontario, Canada. HUInc. distributes copyrighted Health Utilities Index (HUI) materials and provides methodological advice on the use of HUI.

: In the conduct of this study, survey respondents provided electronic click consent after reviewing study information, by agreeing to consent statements and proceeding to the survey.

: Survey respondents were informed that results may be published prior to providing consent to participate.

: De-identified data and study materials are available from the corresponding author on request.

: Fractional factorial design and analysis R code are available from the corresponding author on request.

: KJ, IA, JD, DF, PN, DM, SS, and KG conceived the study, interpreted the results, and prepared the manuscript. KJ, IA, JD, DF, PN, DM, SS, and KG developed/reviewed the survey. KJ analyzed the data. All authors critically reviewed the manuscript and approved the final draft.

: This study received institutional review board (IRB) approval through Advarra, Inc. (Pro00052976). This study was performed in accordance with the Declaration of Helsinki—Version 2008.