Zhang, Rongrong
O’Connell, Thomas
Monteleone, Berrin
Teng, Yixi
Hwu, Paul Wuh-Liang
Castellano, Paul
Tomazos, Ioannis https://orcid.org/0000-0003-0290-4583
Funding for this research was provided by:
PTC Therapeutics
Article History
Received: 17 April 2025
Accepted: 11 September 2025
First Online: 24 September 2025
Declarations
:
: RZ, PC, and IT are employees of PTC Therapeutics Inc. and may be shareholders in the company. TOC and YT are employees of Medicus Economics which was contracted by PTC Therapeutics Inc. for the conduct of this study. PW-HL and BM received consulting fees from PTC Therapeutics Inc.
: The datasets produced during this study are available from the corresponding author upon reasonable request.
: This study used de-identified secondary data, and therefore did not require ethical approval or individual patient consent.
: All authors contributed to the study conception and design. Data analysis was performed by YT and TOC. All authors contributed to the writing of the manuscript. All authors read and approved the final manuscript.
: As the data used in this study were anonymized, participant consent to participate was not necessary.
: As the data used in this study were anonymized, participant consent for publication was not necessary.