Article History
Accepted: 10 August 2023
First Online: 15 August 2023
Declarations
:
: Not applicable.
: Not applicable.
: The authors were recipients of the National Organization for Rare Disorders (NORD) travel/lodging scholarships to attend the NORD 2022 Rare Diseases and Orphan Products Breakthrough Summit. This work is in part inspired by the authors’ experiences at the summit.