Direct Reprogramming of Human DMD Fibroblasts into Myotubes for In Vitro Evaluation of Antisense-Mediated Exon Skipping and Exons 45–55 Skipping Accompanied by Rescue of Dystrophin Expression
Crossref DOI link: https://doi.org/10.1007/978-1-4939-8651-4_8
Published Online: 2018-09-01
Published Print: 2018
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Lee, Joshua J. A.
Saito, Takashi
Duddy, William
Takeda, Shin’ichi
Yokota, Toshifumi
License valid from 2018-01-01
Text and Data Mining valid from 2018-01-01