Antibody-mediated enzyme replacement therapy targeting both lysosomal and cytoplasmic glycogen in Pompe disease
Crossref DOI link: https://doi.org/10.1007/s00109-017-1505-9
Published Online: 2017-02-02
Published Print: 2017-05
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Yi, Haiqing
Sun, Tao
Armstrong, Dustin
Borneman, Scott
Yang, Chunyu
Austin, Stephanie
Kishnani, Priya S.
Sun, Baodong http://orcid.org/0000-0002-2191-0025
Funding for this research was provided by:
Valerion Therapeutics
License valid from 2017-02-02