Adeno-associated viral gene therapy for mucopolysaccharidoses exhibiting neurodegeneration
Crossref DOI link: https://doi.org/10.1007/s00109-017-1562-0
Published Online: 2017-06-29
Published Print: 2017-10
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Lau, Adeline A.
Hemsley, Kim M.
License valid from 2017-06-29