Funding for this research was provided by:
Rare Diseases Clinical Research Network (1U54AR068069–0)
Article History
Received: 20 December 2023
Accepted: 24 January 2024
First Online: 12 March 2024
Declarations
:
: Winnie Liu has nothing to disclose. Lindsey Nicol receives consulting fees from Egetis and Ultragenyx. Eric Orwoll receives consulting fees from Ultragenyx, Angitia, and Amgen.