Tatlisumak, Turgut
Putaala, Jukka
Innilä, Markus
Enzinger, Christian
Metso, Tiina M.
Curtze, Sami
von Sarnowski, Bettina
Amaral-Silva, Alexandre
Jungehulsing, Gerhard Jan
Tanislav, Christian
Thijs, Vincent
Rolfs, Arndt
Norrving, Bo
Fazekas, Franz
Suomalainen, Anu
Kolodny, Edwin H.
Funding for this research was provided by:
Shire Human Genetic Therapies